CureDuchenne

CureDuchenne is a U.S.-based nonprofit organisation dedicated to finding a cure for Duchenne muscular dystrophy (DMD) and improving the lives of those affected by the disease.

Founded by parents after their child was diagnosed with Duchenne, CureDuchenne has grown into a global leader in Duchenne research acceleration, clinical care improvement, and patient advocacy.

The organization operates through a venture philanthropy model, funding early-stage scientific research and biotech innovation, helping promising therapies progress from laboratory research into clinical trials and approved treatments. It also works closely with clinicians, pharmaceutical companies, and academic researchers to accelerate drug development and improve standards of care worldwide.

Beyond research, CureDuchenne provides education, clinical guidance, and support programs for families, including care resources, training for healthcare professionals, and community engagement initiatives. It also helps establish and strengthen specialised Duchenne care clinics to improve long-term patient outcomes.